Unlocking Tomorrows Together
BioMarin continues its more than 25-year history of working towards developing first- or best-in-class therapies for people with rare genetic diseases. Our first approved therapy was inspired by a father who refused to accept that his son’s rare diagnosis lacked a viable therapy. That relentless pursuit to change the course of his son’s future through the power of treatment is still at the core of who we are today.
We focus on rare conditions where we believe we can make a meaningful impact.Learn More about the diseases and conditions we treat ⌃
Each drug candidate we pursue is guided by a fundamental understanding of the genetics and underlying biology of the condition we hope to address.Learn More about our pipline ⌃
We take pride in manufacturing complex therapies for the patients who need them most.Learn More Manufacturing Excellence ⌃